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Facioscapulohumeral Muscular Dystrophy: Genetics and Trials
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A complex combination of molecular pathways and cell interactions causes facioscapulohumeral muscular dystrophy (FSHD). Several new therapies pose a promising solution to this disease with no cure. This chapter aims to explain the genetics of facioscapulohumeral muscular dystrophy, and review the current clinical trials for the treatment of FSHD.
Title: Facioscapulohumeral Muscular Dystrophy: Genetics and Trials
Description:
A complex combination of molecular pathways and cell interactions causes facioscapulohumeral muscular dystrophy (FSHD).
Several new therapies pose a promising solution to this disease with no cure.
This chapter aims to explain the genetics of facioscapulohumeral muscular dystrophy, and review the current clinical trials for the treatment of FSHD.
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